Development of allele-specific therapeutic siRNA for keratin 5 mutations in epidermolysis bullosa simplex

  • Sarah D. Atkinson
  • , Victoria E. McGilligan
  • , Haihui Liao
  • , Ildiko Szeverenyi
  • , Frances J. D. Smith
  • , C. B. Tara Moore
  • , W. H. Irwin McLean

    Research output: Contribution to journalArticlepeer-review

    67 Citations (Scopus)

    Fingerprint

    Dive into the research topics of 'Development of allele-specific therapeutic siRNA for keratin 5 mutations in epidermolysis bullosa simplex'. Together they form a unique fingerprint.

    Keyphrases

    Biochemistry, Genetics and Molecular Biology

    Pharmacology, Toxicology and Pharmaceutical Science

    Immunology and Microbiology