UBA1/GARS-dependent pathways drive sensory-motor connectivity defects in spinal muscular atrophy

Hannah K. Shorrock, Dinja van der Hoorn, Penelope J. Boyd, Maica Llavero Hurtado, Douglas J. Lamont, Brunhilde Wirth, James N. Sleigh, Giampietro Schiavo, Thomas M. Wishart, Ewout J. N. Groen (Lead / Corresponding author), Thomas H. Gillingwater

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28 Citations (Scopus)
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Keyphrases

Neuroscience

Pharmacology, Toxicology and Pharmaceutical Science